Topical Collection on Genome Editing

In this topical collection (18 articles)

1. Genome Editing (SN Waddington, Section Editor)

   Transcription Activator-Like Effector (TALE) Nucleases and Repressor TALEs for Antiviral Gene Therapy

   Kristie Bloom, Claudio Mussolino, Patrick Arbuthnot Pages 1-8

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2. Genome Editing (SN Waddington and TR McKay, Section Editors)

   Barriers to Effective Genome Editing of Haematopoietic Stem Cells

   Steven J. Howe, Michael D. Milsom Pages 2-8

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3. Genome Editing (SN Waddington, Section Editor)

   Genome Editing: Potential Treatment for Lysosomal Storage Diseases

   Talita Giacomet de Carvalho, Ursula da Silveira Matte… Pages 9-15

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4. Genome Editing (SN Waddington and TR McKay, Section Editors)

   A Broad Overview and Review of CRISPR-Cas Technology and Stem Cells

   Simon N. Waddington, Riccardo Privolizzi, Rajvinder Karda… Pages 9-20

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5. Genome Editing (SN Waddington, Section Editor)

   The Potential of AAV-Mediated Gene Targeting for Gene and Cell Therapy Applications

   Ian E. Alexander, David W. Russell Pages 16-22

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6. Genome Editing (SN Waddington, Section Editor)

   Genome Editing of the Blood: Opportunities and Challenges

   Matthew H. Porteus Pages 23-30

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7. Genome Editing (SN Waddington, Section Editor)

   Genome Editing in Stem Cells

   Lorna M. FitzPatrick, Tristan R. McKay Pages 31-38

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8. 

   Genome Editing (Y Fan & J Chan, Section Editors)

   Genome Editing for Rare Diseases

   Arun Pradhan, Tanya V. Kalin, Vladimir V. Kalinichenko Pages 41-51

9. 

   Genome Editing (Y Fan & J Chan, Section Editors)

   In Utero Gene Editing for Inherited Lung Diseases

   Brandon M. White, Edward E. Morrisey, William H. Peranteau Pages 44-52

10. 

    Genome Editing (Y Fan & J Chan, Section Editors)

    In Vivo Genome Engineering for the Treatment of Muscular Dystrophies

    Monika Kustermann, Matthew J. Rok, Ronald D. Cohn… Pages 52-66

11. Genome Editing (SN Waddington and TR McKay, Section Editors)

    The Application of CRISPR/Cas9 Technologies and Therapies in Stem Cells

    Janine Scholefield, Marc S. Weinberg Pages 95-103

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12. Genome Editing (SN Waddington and HC O'Neill, Section Editors)

    Harnessing the Potential of Human Pluripotent Stem Cells and Gene Editing for the Treatment of Retinal Degeneration

    Patrick Ovando-Roche, Anastasios Georgiadis… Pages 112-123

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13. Genome Editing (SN Waddington and HC O'Neill, Section Editors)

    Genome-Edited T Cell Therapies

    Juliette M. K. M. Delhove, Waseem Qasim Pages 124-136

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14. Genome Editing (Y Fan & J Chan, Section Editors)

    Responsible Translational Pathways for Germline Gene Editing?

    Bryan Cwik Pages 126-133

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15. Genome Editing (SN Waddington and HC O'Neill, Section Editors)

    Genome Editing and Muscle Stem Cells as a Therapeutic Tool for Muscular Dystrophies

    Veronica Pini, Jennifer E. Morgan, Francesco Muntoni… Pages 137-148

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16. 

    Genome Editing (SN Waddington and HC O'Neill, Section Editors)

    Gene Editing of Stem Cells to Model and Treat Disease

    Jennifer A. Hollywood, David J. Sanz, Alan J. Davidson… Pages 253-263

17. 

    Genome Editing (SN Waddington and HC O'Neill, Section Editors)

    Mini Review: Application of Human Mesenchymal Stem Cells in Gene and Stem Cells Therapy Era

    Ruixia Deng, Anna Hing Yee Law, Jiangang Shen… Pages 327-337

18. 

    Genome Editing (SN Waddington and HC O'Neill, Section Editors)

    Editing the Genome Ex Vivo Stem Cell Therapy

    Yi** Fan, Jerry Kok Yen Chan Pages 338-345