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  1. Article

    Open Access

    A Broad Overview and Review of CRISPR-Cas Technology and Stem Cells

    The pinnacle of four decades of research, induced pluripotent stem cells (iPSCs), and genome editing with the advent of clustered, regularly interspaced, short palindromic repeats (CRISPR) now promise to take ...

    Simon N. Waddington, Riccardo Privolizzi, Rajvinder Karda… in Current Stem Cell Reports (2016)

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  2. Article

    Open Access

    Impaired cellular bioenergetics caused by GBA1 depletion sensitizes neurons to calcium overload

    Heterozygous mutations of the lysosomal enzyme glucocerebrosidase (GBA1) represent the major genetic risk for Parkinson’s disease (PD), while homozygous GBA1 mutations cause Gaucher disease, a lysosomal storage d...

    Nicoletta Plotegher, Dany Perocheau, Ruggero Ferrazza… in Cell Death & Differentiation (2020)

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  3. Article

    Open Access

    Correction: Impaired cellular bioenergetics caused by GBA1 depletion sensitizes neurons to calcium overload

    An amendment to this paper has been published and can be accessed via a link at the top of the paper.

    Nicoletta Plotegher, Dany Perocheau, Ruggero Ferrazza… in Cell Death & Differentiation (2020)

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