Skip to main content

and
  1. Article

    Open Access

    Correction to: Pharmacokinetic and Pharmacodynamic Properties of Cemdisiran, an RNAi Therapeutic Targeting Complement Component 5, in Healthy Subjects and Patients with Paroxysmal Nocturnal Hemoglobinuria

    Prajakta Badri, Xuemin Jiang, Anna Borodovsky, Nader Najafan in Clinical Pharmacokinetics (2022)

  2. Article

    Open Access

    Pharmacokinetic and Pharmacodynamic Properties of Cemdisiran, an RNAi Therapeutic Targeting Complement Component 5, in Healthy Subjects and Patients with Paroxysmal Nocturnal Hemoglobinuria

    Cemdisiran, an N-acetylgalactosamine (GalNAc) conjugated RNA interference (RNAi) therapeutic, is currently under development for the treatment of complement-mediated diseases by suppressing liver production of co...

    Prajakta Badri, Xuemin Jiang, Anna Borodovsky, Nader Najafian in Clinical Pharmacokinetics (2021)