Skip to main content

6 Result(s)

within Sheila Shapouri Remove this filter

and

  1. Article

    Open Access

    Adherence and Persistence Among Risdiplam-Treated Individuals with Spinal Muscular Atrophy: A Retrospective Claims Analysis

    Spinal muscular atrophy (SMA) is a neuromuscular disease caused by deletions and/or mutations in the survival of motor neuron 1 (SMN1) gene. Risdiplam, the first and only oral SMN2 pre-mRNA splicing modifier, is ...

    Elmor D. Pineda, Tu My To, Travis L. Dickendesher, Sheila Shapouri… in Advances in Therapy (2024)

    Download PDF (665 KB) View Article

  2. Article

    Open Access

    Budget Impact of Introducing Fixed-Duration Mosunetuzumab for the Treatment of Relapsed or Refractory Follicular Lymphoma After Two or More Lines of Systemic Therapy in the USA

    This study aimed to assess the budget impact of introducing fixed-duration mosunetuzumab as a treatment option for adult patients with relapsed or refractory follicular lymphoma after at least two prior system...

    Shih-Wen Lin, Sheila Shapouri, Hélène Parisé, Eric Bercaw, Mei Wu… in PharmacoEconomics (2024)

    Download PDF (1241 KB) View Article

  3. Article

    Open Access

    Assessing the impact of grief on quality of life, work productivity, and health outcomes for parents bereaved from SMA: A study protocol

    U.S. cost-effectiveness recommendations suggest that analyses should include all costs and effects relevant to the decision problem [1]. However, in many diseases, including spinal muscular atrophy (SMA), few stu...

    Abigail G. Riley, Christina M. Mulé… in Cost Effectiveness and Resource Allocation (2023)

    Download PDF (704 KB) View Article

  4. Article

    Open Access

    Budget Impact of 12-Month Fixed Treatment Duration Venetoclax in Combination with Obinutuzumab in Previously Untreated Chronic Lymphocytic Leukemia Patients in the United States

    This study aimed to assess the total cost of care (TCC) and budget impact of introducing 12-month fixed duration venetoclax + obinutuzumab (VEN+G) as first-line treatment for chronic lymphocytic leukemia (CLL)...

    Sang Kyu Cho, Beenish S. Manzoor, Kavita R. Sail, Hélène Parisé… in PharmacoEconomics (2020)

    Download PDF (1299 KB) View Article

  5. No Access

    Article

    A comprehensive transcriptional map of primate brain development

    The transcriptional underpinnings of brain development remain poorly understood, particularly in humans and closely related non-human primates. We describe a high-resolution transcriptional atlas of rhesus mon...

    Trygve E. Bakken, Jeremy A. Miller, Song-Lin Ding, Susan M. Sunkin… in Nature (2016)

  6. No Access

    Article

    Transcriptional landscape of the prenatal human brain

    The anatomical and functional architecture of the human brain is mainly determined by prenatal transcriptional processes. We describe an anatomically comprehensive atlas of the mid-gestational human brain, inc...

    Jeremy A. Miller, Song-Lin Ding, Susan M. Sunkin, Kimberly A. Smith, Lydia Ng… in Nature (2014)