7 Result(s)
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Waseem Qasim
Internal Medicine
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Article
Open AccessNon-osteopenic Bone Pathology After Allo-hematopoietic Stem Cell Transplantation in Patients with Inborn Errors of Immunity
There is a lack of data on post-HSCT non-osteopenic bone pathology specifically for children with inborn errors of immunity (IEI). We collected data on non-osteopenic bone pathology in children with IEI post-H...
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Chapter
Off-the-Shelf Allogeneic CAR-T Cells or Other Immune Effector Cells
“Off-the-shelf” allogeneic CAR TCRab T cells and other immune effector cells, such as natural killer (NK) or gamma delta (gd) T cells, can be premanufactured from healthy donors and may offer alternatives to a...
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Article
Open AccessBase-edited CAR T cells for combinational therapy against T cell malignancies
Targeting T cell malignancies using chimeric antigen receptor (CAR) T cells is hindered by ‘T v T’ fratricide against shared antigens such as CD3 and CD7. Base editing offers the possibility of seamless disrup...
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Article
Outcome of Non-hematological Autoimmunity After Hematopoietic Cell Transplantation in Children with Primary Immunodeficiency
Knowledge of post-hematopoietic cell transplantation (HCT) non-hematological autoimmune disease (AD) is far from satisfactory.
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Article
Hematopoietic stem cell transplantation for cytidine triphosphate synthase 1 (CTPS1) deficiency
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Article
Variable Phenotype of Severe Immunodeficiencies Associated with RMRP Gene Mutations
Mutations in RMRP primarily give rise to Cartilage Hair Hypoplasia (CHH), a highly diverse skeletal disorder which can be associated with severe immunodeficiency. Increased availability of RMRP mutation screening...
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Article
Gene Therapy for Primary Immunodeficiencies: Current Status and Future Prospects
Gene therapy using autologous haematopoietic stem cells offers a valuable treatment option for patients with primary immunodeficiencies who do not have access to an HLA-matched donor, although such treatments ...
