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  1. Article

    Open Access

    Eteplirsen Treatment for Duchenne Muscular Dystrophy: A Qualitative Patient Experience Study

    Duchenne muscular dystrophy (DMD) is characterized by rapid functional decline. Current available treatment options aim to delay disease progression or stabilize physical function. To aid in healthcare provide...

    Joel Iff, Chloe Carmichael, Stephanie McKee, Ihor Sehinovych in Advances in Therapy (2024)