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  1. Article

    Open Access

    Long term follow-up after haematopoietic stem cell transplantation for mucopolysaccharidosis type I-H: a retrospective study of 51 patients

    Mucopolysaccharidosis type I-H (MPS I-H) is a rare lysosomal storage disorder caused by α-L-Iduronidase deficiency. Early haematopoietic stem cell transplantation (HSCT) is the sole available therapeutic optio...

    Antoine Gardin, Martin Castelle, Samia Pichard, Aline Cano in Bone Marrow Transplantation (2023)

  2. No Access

    Article

    Recent results of hematopoietic stem cell transplantation for thalassemia with busulfan-based conditioning regimen in France: improved thalassemia free survival despite frequent mixed chimerism. A retrospective study from the Francophone Society of Stem Cell Transplantation and Cellular Therapy (SFGM-TC)

    Marica Rossi, Sarah Szepetowski, Karima Yakouben in Bone Marrow Transplantation (2023)

  3. No Access

    Article

    Efficacy of eculizumab in transplantation-associated thrombotic microangiopathy: results of the French nationwide study on behalf of the SFGM-TC and the CNR-MAT

    Marion Peyre, Flore Sicre de Fontbrune, Ana Berceanu in Bone Marrow Transplantation (2024)