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  1. Article

    Open Access

    Motor function in type 2 and 3 SMA patients treated with Nusinersen: a critical review and meta-analysis

    There is an increasing number of papers reporting the real world use of Nusinersen in different cohorts of SMA patients.

    Giorgia Coratti, Costanza Cutrona, Maria Carmela Pera in Orphanet Journal of Rare Diseases (2021)